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determined the efficiency of gene editing for PKU gene therapy in vivo
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创建时间：
2019-05-25
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Supplementary data for: Phenylketonuria in a microbial world, chapter 3
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In vivo genome editing restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers [WES]
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Cardiomyocyte-Specific Expression of Lamin A Improves Cardiac Function in Lmna −/− Mice
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