Picking the right target for HSC-mediated gene therapy
收藏NIAID Data Ecosystem2026-05-26 收录
官方服务：
资源简介：
Hematopoietic stem cell (HSC)-mediated gene therapy holds enormous potential for the treatment of hematological diseases and disorders. However, most strategies target CD34+ cells, a heterogeneous mix of predominantly committed progenitors and only very few multipotent HSCs. Consequently, the HSC targeting efficiency is low, the long-term outcome poor and currently available approaches very costly.
创建时间：
2019-03-31
